cGMP Manufacturing Process Development & Preparation of Pre-IND Briefing Package for an AAV Gene Therapy Targeting Mucopolysaccharidosis Type I
NCBiotech Grants & Loans
See the full listing of all NCBiotech grants and loans awarded since July 2012.
Organization
RainBIO, Inc.
Award Date
Award Amount
250,000
Program Name
Small Business Research Loan
Program Category
Business Financing
Principal Investigator
Frances Martin
Fiscal Year
2021
Region
Research Triangle
Project Description:
RainBio Inc. is utilizing a recombinant adeno-associated (rAAV) gene therapy strategy to prevent and reverse loss of vision frequently associated with lysosomal storage disorders. The company was awarded a $250k SRL to support the initial stages of process development, cGMP manufacturing and preparation for IND submission.