Gene Therapy of ATP1A3 Related Disease
NCBiotech Grants & Loans
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Organization
Duke University Medical Center
Award Date
Award Amount
109,845
Program Name
Translational Research Grant
Program Category
Research and Equipment Support
Principal Investigator
Mohamad Mikati
Fiscal Year
2023
Region
Research Triangle
Project Description:
Researchers at Duke University are investigating a gene therapy treatment for Alternating Hemiplegia of Childhood (AHC), which is a debilitating disease that often results in pain, developmental delays, and early death.